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Sign up to view this video Join Now Trial Design, • 9/22/25 Accelerating Rare Disease Therapies: Strategies for Efficient Clinical Development Next Adaptive & Precision-Driven Trials: Platform and MATCH Models for Rare Disease Breakthroughs You Might Also Like How To Prevent Failure in Rare Disease Trials? How to Accelerate the Adoption of Decentralized Trials for Rare Disease Indications Ethics and Strategies for Returning Individual Patient Data Collected in Clinical Research Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials Aligning Trials with Patient-Lived Experiences