Sign up to view this video Join Now Closing Panel, • 9/22/25 Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials Previous Case Studies in Rare Disease Commercialization: Lessons Learned You Might Also Like Real-World Evidence That Matters: A Hands-On Workshop in Building Credible Value Stories AI-Driven Patient Identification and Recruitment Adaptive & Precision-Driven Trials: Platform and MATCH Models for Rare Disease Breakthroughs Decentralized by Design: Operationalizing Hybrid Rare Disease Trials Opening Keynote: The Future of Rare Disease Trials
Sign up to view this video Join Now Closing Panel, • 9/22/25 Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials Previous Case Studies in Rare Disease Commercialization: Lessons Learned You Might Also Like Real-World Evidence That Matters: A Hands-On Workshop in Building Credible Value Stories AI-Driven Patient Identification and Recruitment Adaptive & Precision-Driven Trials: Platform and MATCH Models for Rare Disease Breakthroughs Decentralized by Design: Operationalizing Hybrid Rare Disease Trials Opening Keynote: The Future of Rare Disease Trials
