Sign up to view this video Join Now Closing Panel, • 9/22/25 Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials You Might Also Like Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials Case Studies in Rare Disease Commercialization: Lessons Learned Opening Keynote: The Evolving Regulatory Environment for Rare Disease Trials Conducting Rare Disease Clinical Trials to Support Market Access and Commercialization Patient Recruitment and Engagement in in Global, Multisite Rare Disease Trials
Sign up to view this video Join Now Closing Panel, • 9/22/25 Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials You Might Also Like Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials Case Studies in Rare Disease Commercialization: Lessons Learned Opening Keynote: The Evolving Regulatory Environment for Rare Disease Trials Conducting Rare Disease Clinical Trials to Support Market Access and Commercialization Patient Recruitment and Engagement in in Global, Multisite Rare Disease Trials