Rare Disease Chief Medical Officer Council

2:00 - 5:00 pm EST on September 9, 2025

(Limited to 30 Participants)

Top Reasons to Attend

Peer-to-Peer Insight Exchange

You face highly specialized, high-stakes decisions. This session offers a trusted, closed-door forum to share real-world experiences, challenges, and strategies with peers navigating similar regulatory, clinical, and commercial hurdles.

Strategic Collaboration Opportunities

With limited patient populations and overlapping investigator and advocacy networks, rare disease development thrives on collaboration. The session offers structured networking that could lead to co-development, licensing, or data-sharing opportunities.

Practical Solutions to Unsolved Challenges

Unlike large conferences, this session can be tailored to address operational bottlenecks and emerging concerns that CMOs are actively grappling with—such as clinical trial recruitment, FDA interactions, or long-term follow-up burdens.

CMO Council Agenda

02:00 PM – 2:20 PM | Welcome & Introductions — Framing the purpose: candid peer discussion and idea exchange

02:20 PM – 03:00 PM | Topic 1: Topic 1: Smart Trial Design for Small Populations — Case-based discussion: adaptive trials, natural history controls, and endpoints that matter.

03:00 PM – 03:20 PM | Networking Break

03:20 PM – 04:00 PM | Topic 2: The CMO’s Role in Accelerating Approval & Launch — Sharing strategies on regulatory navigation, cross-functional team building, and launch readiness.

04:00 PM – 04:15 PM | Networking Break

04:15 PM – 04:55 PM | Topic 3: Collaborating to Solve the Recruitment Bottleneck — What’s working in rare disease trials? Decentralized models, patient travel, advocacy partnerships.

04:55 PM – 05:00 PM | Closing & Key Insights Recap

05:00 PM – 7:00 PM | Exhibitor Reception (Exhibit Hall)