Sign up to view this video Join Now Clinical Operations, • 9/22/25 Purpose-Driven Metrics: Running Gene Therapy Trials with KPIs That Matter Previous Beyond the Feasibility Survey: Strategic Site Selection to Accelerate Trials and Optimize Resources You Might Also Like Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials Operationalizing Precision Medicine in Rare Disease Trials Adaptive & Precision-Driven Trials: Platform and MATCH Models for Rare Disease Breakthroughs Patient-Centric Commercialization: Integrating Patient Voices into Market Access Strategies Aligning Trials with Patient-Lived Experiences
Sign up to view this video Join Now Clinical Operations, • 9/22/25 Purpose-Driven Metrics: Running Gene Therapy Trials with KPIs That Matter Previous Beyond the Feasibility Survey: Strategic Site Selection to Accelerate Trials and Optimize Resources You Might Also Like Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials Operationalizing Precision Medicine in Rare Disease Trials Adaptive & Precision-Driven Trials: Platform and MATCH Models for Rare Disease Breakthroughs Patient-Centric Commercialization: Integrating Patient Voices into Market Access Strategies Aligning Trials with Patient-Lived Experiences