2025 Rare Trials Summit Skip to Videos All | Opening Keynotes | Trial Design | Patient Voice | Clinical Operations | Commercialization | Closing Panel | How To Prevent Failure in Rare Disease Trials? Patient Recruitment and Engagement in in Global, Multisite Rare Disease Trials Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials Optimizing CRO and Vendor Selection - Examples from the Field Beyond the Feasibility Survey: Strategic Site Selection to Accelerate Trials and Optimize Resources Purpose-Driven Metrics: Running Gene Therapy Trials with KPIs That Matter
